Rare Glycogen Storage Diseases Natural History Study
Analysis of Clinical features and Echocardiographic / ML algorithms (includes rare cardiomyopathies)
Healthcare Utilization and Economic Burden of Cardiomyopathy in China
Natural History of Danon Disease
The Natural History of Danon Disease
Danon Disease Natural History Study
A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease
Gene Therapy for Male Patients With Danon Disease Using AAV9.LAMP2B (RP-A501)
LAMP2 microdeletions in patients with Danon disease
Danon disease: diagnosis made by cardiac magnetic resonance