Clinical Trials

Clinical trials are conducted to determine the safety and effectiveness of medicines.

Clinical research plays a vital role in advancing medicine. It is essential for scientists, the companies who develop therapies and healthcare professionals – and most importantly, for patients. Patient involvement is essential to ensure that new approaches are studied responsibly and reflect real-life experiences.

Clinical Studies and Gene Therapy Trials

Join a Danon disease clinical study that contributes to research on new potential therapies.

LAMPLIGHT-NH Natural History is an observational study to collect the medical history and day-to-day experiences of people with Danon disease to provide researchers a greater understanding of this condition.

LAMPLIGHT-2 Gene Therapy is an interventional study for Danon disease, with the gene therapy designed to deliver a functional LAMP2 gene into a patient’s cells to replace the damaged gene.

Learn more

Global Heart Hub Clinical Research Initiative

The Danon Foundation recognizes the leadership of the Global Heart Hub Clinical Research Initiative in building patient-focused education and tools to support the understanding of clinical trials. Their work has helped make clinical research more accessible, understandable and relevant to people living with heart disease around the world. We are committed to providing education and meaningful engagement in research, and we are open to collaboration with Global Heart Hub and other partners to strengthen patient-centered clinical research in Danon disease.

As part of our affiliation with Global Heart Hub, we are sharing a user-friendly Clinical Research Portal, adapted to multiple languages, with trials available in individual countries.

Search for Clinical trials below: